Inherited Muscle Diseases
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Inherited Muscle Diseases trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Inherited Muscle Diseases trials you may qualify forThe goal of this clinical trial is to evaluate the impact of using the Nomad powered KAFO in people who have had a musculoskeletal or neurological injury that h…
The purpose of the study is to evaluate the safety, tolerability, and efficacy of the two different treatment combinations of tulmimetostat in participants with…
People with cerebral palsy (CP), muscular dystrophy (MD), spina bifida, or spinal cord injury often have muscle weakness, and problems moving their arms and leg…
The Duchenne Registry is an online, patient-report registry for individuals with Duchenne and Becker muscular dystrophy and carrier females. The purpose of the…
The phase I portion of this study is designed for children or adolescents and young adults (AYA) with a diagnosis of a solid tumor that has recurred (come back…
This study aims to compare the effects of hip-based and knee-based exercise interventions on medial longitudinal arch height, dynamic balance, and lower limb mu…
This open-label, single-arm study will evaluate the safety and expression of delandistrogene moxeparvovec in participants with DMD. Participants will be in the…
Children with Down syndrome often exhibit diminished physical fitness levels and lower bone mass. Numerous factors contribute to this decrease in bone mass dens…