Inherited Mitochondrial Disease, Including Leigh Syndrome

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Inherited Mitochondrial Disease, Including Leigh Syndrome trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

All recent trials (1 shown)

CompletedPhase 2

NCT02023866

Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease

To evaluate safety, tolerability and efficacy of cysteamine bitartrate delayed-release capsules (RP103) administered at a target maintenance dose of 1.3 g/m²/da…

United States36 participantsStarted 2014-05

Treatment: Cysteamine Bitartrate