Inherited Metabolic Disorders IMD

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Inherited Metabolic Disorders IMD trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 2 trials

RecruitingNot Applicable

NCT04528355

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

This is a data collection study that will examine the general diagnostic and treatment data associated with the reduced-intensity chemotherapy-based regimen pai…

United States50 participantsStarted 2020-08-20

Treatment: data collection

RecruitingPhase 2

NCT01962415

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

The objective of this study is to evaluate the efficacy of using a reduced-intensity condition (RIC) regimen with umbilical cord blood transplant (UCBT), double…

United States100 participantsStarted 2014-02-04

Treatment: Hydroxyurea, Alemtuzumab

All recent trials (6 shown)

Active — Not RecruitingPhase 2

NCT02171104

MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

This single-institution, phase II study is designed to test the ability to achieve donor hematopoietic engraftment while maintaining low rates of transplant-rel…

United States149 participantsStarted 2014-07-10

Treatment: Stem Cell Transplantation, IMD Preparative Regimen

CompletedPhase 2

NCT03406962

MGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HSCT)

This study is designed to assess the safety and efficacy of using MGTA-456 in patients with Inherited Metabolic Disorders (IMD) undergoing stem cell transplanta…

United States8 participantsStarted 2018-02-09

Treatment: MGTA-456

Inherited Metabolic Disorders IMD

Trial phase breakdown

Trial status

Actively recruiting — 2 trials

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

All recent trials (6 shown)

MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

MGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HSCT)

Trial phase breakdown

Trial status

Actively recruiting — 2 trials

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

All recent trials (6 shown)

MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

MGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HSCT)

A Follow-up Study in Patients With Inherited Metabolic Disorders (IMD) Who Underwent Hematopoietic Stem Cell Transplanta…

Safety and Exploratory Efficacy of HSC835 in Patients With Inherited Metabolic Disorders (IMD)