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Infantile Refsum's Disease
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Infantile Refsum's Disease trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Infantile Refsum's Disease trials may be worth asking aboutNorth America
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This single-institution, phase II study is designed to test the ability to achieve donor hematopoietic engraftment while maintaining low rates of transplant-rel…
OBJECTIVES: I. To Evaluate the therapeutic efficacy of cholic acid during provision of compassionate treatment to patients with identified inborn errors of bil…