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Infantile Globoid Cell Leukodystrophy
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Infantile Globoid Cell Leukodystrophy trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Infantile Globoid Cell Leukodystrophy trials may be worth asking aboutNorth America
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This single-institution, phase II study is designed to test the ability to achieve donor hematopoietic engraftment while maintaining low rates of transplant-rel…
This is a non-blinded, non-randomized dose escalation study of intravenous FBX-101 in which subjects will receive a single infusion of an adeno-associated virus…
PBKR03 is a gene therapy for Krabbe Disease (Globoid cell leukodystrophy) intended to deliver a functional copy of the GALC gene to the brain and peripheral tis…
The objective of this study is to evaluate the natural history of disease progression in infants with globoid cell leukodystrophy (GLD).
The purpose of this natural history study is to understand more about the progression of infantile Krabbe disease, a very rare genetic disease. There is very li…