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Giant Axonal Neuropathy
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Giant Axonal Neuropathy trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
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Title: Intrathecal Administration of scAAV9/JeT-GAN for the Treatment of Giant Axonal Neuropathy Background: \- The Gigaxonin gene lets the body make a protei…
Giant Axonal Neuropathy (GAN) is a devastating and rare childhood disease. Children with GAN develop increasing muscle weakness, impaired sensation, and at time…