Gamma-sarcoglycanopathy

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Gamma-sarcoglycanopathy trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingNot Applicable

NCT05989620

Long-Term Development of Muscular Dystrophy Outcome Assessments

This is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset P…

United States1,000 participantsStarted 2023-10-18

All recent trials (12 shown)

Active — Not RecruitingPhase 1

NCT05973630

ATA-200 Gene Therapy Trial in Patients With LGMDR5

The purpose of ATA-003-GSAR study is to evaluate the safety and tolerability of a single intravenous infusion of ATA-200 in pediatric patients with limb girdle…

United States4 participantsStarted 2025-02-15

Treatment: ATA-200

Active — Not RecruitingNot Applicable

NCT04475926

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who…

This study will follow participants who are screened and confirmed with a genetic diagnosis of Limb-girdle muscular dystrophy type 2E (LGMD2E/R4), Limb-girdle m…

United States205 participantsStarted 2021-04-22

Gamma-sarcoglycanopathy

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

Long-Term Development of Muscular Dystrophy Outcome Assessments

All recent trials (12 shown)

ATA-200 Gene Therapy Trial in Patients With LGMDR5

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who…

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

Long-Term Development of Muscular Dystrophy Outcome Assessments

All recent trials (12 shown)

ATA-200 Gene Therapy Trial in Patients With LGMDR5

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who…

Natural History Study in Patients With LGMDR5/2c

A Study of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Pediatric and Adult Participants

Impact of Clinical Pharmacy Services on Medication Cost and Hospitalization Rates in Hemodialysis Patients

Safety and Tolerability of Frovatriptan to Prevention of Menstrually Associated Migraine (MAM) Headaches

Influence of Endothelial Function on Central and Peripheral Causes Of Exercise Impairment in Type 2 Diabetes

Efficacy and Safety Study of Lenalidomide Plus R-CHOP Chemotherapy Versus Placebo Plus R-CHOP Chemotherapy in Untreated…

What Makes Exercise Feel More Difficult to Women With and Without Type 2 Diabetes

Stem Cell Quantification In Peripheral Blood After Hyperbaric Oxygen Therapy Treatments

Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C