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Dwarfism
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Dwarfism trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Dwarfism trials may be worth asking aboutNorth America
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Trials may have sites in multiple countries. Filtering shows any trial with at least one site in the selected country.
The OraGrowtH Phase 3 Trial is a multi-national trial. The goals of the trial are to study LUM-201 as a treatment for Pediatric Growth Hormone Deficiency (PGHD)…
This study aims to investigate how different types and intensities of exercise affect muscle recovery in individuals taking statin medications compared to healt…
Background: There are 461 conditions that affect the bones (skeletal disorders). Many of these are not well understood and do not have any specific treatments.…
This basket trial will enroll prepubertal children and adolescents with clinically diagnosed and genetically confirmed (if applicable) TS, SHOX-D, SGA, or ISS b…
Study 111-903 will generate baseline growth data in children with ISS by collecting growth measurements and other variables of interest.
This is a Phase 2, multicenter, randomized, placebo-controlled study to evaluate the safety and efficacy of infigratinib in participants \< 3 years old with ACH…
This is a multi-center, prospective, parallel-group, open-label, randomized clinical study in one hundred and twenty-six (126) neonates and infants diagnosed wi…
Four rare genetic diseases, xeroderma pigmentosum (XP), Cockayne syndrome (CS), the XP/CS complex and trichothiodystrophy (TTD) have defective DNA excision repa…