Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingPhase 1/2

NCT07429240

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

The purpose of this Phase 1/2a trial is to evaluate the safety, tolerability, and preliminary efficacy of PBGENE-DMD in patients with DMD harboring mutations am…

United States18 participantsStarted 2026-04-24

Treatment: PBGENE-DMD (IV)

Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

All recent trials (1 shown)

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

All recent trials (1 shown)