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Crigler-Najjar Syndrome
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Crigler-Najjar Syndrome trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Crigler-Najjar Syndrome trials may be worth asking aboutNorth America
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This is a Phase 1/2, multinational, open-label, study to evaluate the safety and efficacy of an intravenous infusion of GT-UGT1A1-AAV8-02 in patients with Crigl…
Clinical trial rationale: CNS is an ultra-rare (\<1/1 million newborns), autosomal recessive disorder of bilirubin conjugation caused by mutation in the gene c…
This is a Phase 1/2, multinational, open-label, study to evaluate the safety and efficacy of an intravenous infusion of GNT0003 in patients with Crigler-Najjar…
Newborn screening (NBS) is a global initiative of systematic testing at birth to identify babies with pre-defined severe but treatable conditions. With a simple…
All patients having received at least one infusion of the Investigational Medicinal Product (IMP) HepaStem HHALPC during a previous interventional clinical stud…
The purpose of this research study is to determine whether partial irradiation of the liver and liver cell transplantation can provide help for patients with li…