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CLN6
Clinical trial pipeline · Data from ClinicalTrials.gov
See which CLN6 trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which CLN6 trials you may qualify forThis study aims to assess the natural history of Batten disease (Neuronal Ceroid Lipofuscinosis) by obtaining information about the motor, behavioral, and funct…
This is an observational study that aims at assessing the natural history of NCL diseases as part of the international DEM-CHILD Database. 1. Patient data are…
This is a phase 1/2, open-label, single dose study to evaluate the safety and efficacy of AT-GTX-501 delivered intrathecally into the lumbar spinal cord region…
This is a long-term safety and efficacy study in subjects with CLN6 Batten disease who previously received a single intrathecal administration of AT-GTX-501.
This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective…