Classical Galactosaemia
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Classical Galactosaemia trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Classical Galactosaemia trials you may qualify forA critical knowledge gap is whether proactive intervention can improve speech and language outcomes in infants at known risk for communication disorders. Speech…
This study is designed to assess the clinical benefit as well as the safety, pharmacokinetics (PK), and pharmacodynamics (PD) (reduction of galactitol levels) o…
This study is a first-in-human, randomized, placebo-controlled, 4-Part, single ascending dose (SAD) and multiple ascending dose (MAD) study in healthy adult sub…