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Biallelic RPE65 Mutation-associated Retinal Dystrophy
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Biallelic RPE65 Mutation-associated Retinal Dystrophy trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Biallelic RPE65 Mutation-associated Retinal Dystrophy trials may be worth asking aboutNorth America
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The purpose of this study is to provide safety and efficacy data for voretigene neparvovec, administered as subretinal injection, in Japanese patients with bial…
The purpose of the study is to evaluate the safety, tolerability and efficacy of LX101 in subjects with biallelic RPE65 mutation-associated inherited retinal dy…