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Aromatic L-Amino Acid Decarboxylase Deficiency
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Aromatic L-Amino Acid Decarboxylase Deficiency trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Aromatic L-Amino Acid Decarboxylase Deficiency trials may be worth asking aboutNorth America
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The overall objective of this study is to determine the safety and efficacy of AAV2-hAADC delivered to the substantia nigra pars compacta (SNc) and ventral tegm…
This early Phase trial is to prove the safety and efficacy of VGN-R09b to treat patients with AADC deficiency.
This study will have a trial phase, extension phase, and a long-term extension phase. The primary objectives of the trial phase are to assess the pharmacodynami…
This trial includes dose-escalating part (phase 1) and dose confirming part, to prove the safety and efficacy of VGN-R09b to treat patients with severe AADC def…