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Adrenal Insufficiency, Congenital
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Adrenal Insufficiency, Congenital trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Adrenal Insufficiency, Congenital trials you may qualify forThis study will evaluate and gather information in patients with genetic causes of too much androgen (male-like hormone) in order to better understand the effec…
The study investigators are interested in learning more about how drugs, that are given to children by their health care provider, act in the bodies of children…
This is a data collection study that will examine the general diagnostic and treatment data associated with the reduced-intensity chemotherapy-based regimen pai…
The objective of this study is to evaluate the efficacy of using a reduced-intensity condition (RIC) regimen with umbilical cord blood transplant (UCBT), double…
This protocol aims to gather information about sphingosine phosphate lyase insufficiency syndrome (SPLIS), also known as NPHS14, and to create a SPLIS patient r…
The Myelin Disorders Biorepository Project (MDBP) seeks to collect and analyze clinical data and biological samples from leukodystrophy patients worldwide to su…
Children with congenital primary and secondary adrenal insufficiency, who are deficient in cortisol, are at risk for hypoglycaemia, irrespective of appropriate…
The investigators recently observed that up to 25% of women with X-linked adrenoleukodystrophy (ALD) have moderate to severe Restless Leg Syndrome (RLS). In thi…
The objective of this study is to make T-cell depleted stem cells from a family member who is a half match (haplo-identical) available on an expanded access bas…