Back to search
Adenosine Deaminase Deficiency
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Adenosine Deaminase Deficiency trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Adenosine Deaminase Deficiency trials you may qualify forThe aim of this study is to assess the safety and efficacy of autologous transplantation of hematopoietic stem cells (CD34+ cells) from mobilized peripheral blo…
This is a Phase I/II trial of in vivo lentiviral gene therapy for treating adenosine deaminase severe combined immunodeficiency (ADA-SCID) using a self-inactiva…
Background: Pyrimidine and purine metabolism disorders (DPPMs) affect how the body metabolizes chemicals called pyrimidines and purines. DPPMs can cause dysfun…
This observational long-term follow-up study is designed to collect safety and efficacy data from ADA-SCID patients previously treated with autologous ex vivo g…
Early Check provides voluntary screening of newborns for a selected panel of conditions. The study has three main objectives: 1) develop and implement an approa…