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Porphyrias
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Porphyrias trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Porphyrias trials you may qualify forThe purpose of this study is to collect information about the effects of EPP/XLP in adults and adolescents. This is an observational study in which participants…
This global patient registry is being conducted to characterize the natural history and real-world clinical management of patients with AHP, and to further char…
The main aim of this clinical trial is to learn about the effect of carbohydrate-rich diet as a treatment for AIP (acute intermittent porphyria). Aim: Investig…
This is a study to investigate the effect of oral ATL-001 (ciclopirox) in CEP (Congenital Erythropoietic Porphyria) patients. During the study, it will be measu…
The objective of this protocol is to conduct a longitudinal multidisciplinary investigation of the human porphyrias including the natural history, morbidity, pr…
This study proposes to identify the predisposing/protective modifying genes that underlie the acute attacks in symptomatic patients with Acute Intermittent Porp…
To investigate the efficacy of MT-7117 on time to onset and severity of first prodromal symptoms (burning, tingling, itching, or stinging) associated with sunli…
The goal of this clinical trial is to learn if bitopertin works and is safe to treat EPP or XLP in participants 12 years or older. The main questions it aims to…
The purpose of this study is to evaluate the concentration of afamelanotide in serum after the administration of afamelanotide in adolescent and adult EPP patie…