Neurocutaneous Syndromes
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Neurocutaneous Syndromes trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Neurocutaneous Syndromes trials may be worth asking aboutNorth America
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As part of a post-approval commitment, the Korean health authority requests a study to characterize safety and effectiveness in patients treated with Koselugo (…
This study will collect medical records, scan results, and complete surveys to create a registry about people with a neurofibromatosis type 1-associated brain t…
.Neurofibromatosis type 2 is an inherently autosomal dominant genetic disease, but cases of mosaicism or de novo mutation are not uncommon. the prevalence is es…
To collect information from patients with vHL disease. Information collected will include data on the status of the disease, any surgeries or therapies patients…
This is a study to evaluate the efficacy and safety of belzutifan monotherapy in participants with advanced pheochromocytoma/paraganglioma (PPGL), pancreatic ne…
This study aims to evaluate the burden and phenotypic spectrum of periodontal disease in patients with rare kidney disorders (such as Alport syndrome, Fabry dis…
This study will monitor for potential chronic liver injury and liver fibrosis, in participants treated with cannabidiol oral solution.
A roll-over study to assess long-term effect in pediatric patients treated with dabrafenib and/or trametinib.