CompletedNot Applicable

Longitudinal Characterization of Respiratory Tract Exacerbations and Treatment Responses in Primary Ciliary Dyskinesia

United States105 participantsStarted 2022-03-29

Plain-language summary

The overall objective of this longitudinal, observational study is to provide information needed to inform the design of future interventional trials of respiratory exacerbation prevention and treatment in children and adults with primary ciliary dyskinesia (PCD).

Who can participate

Age range6 Years

SexALL

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Inclusion criteria

✓. Clinical features consistent with PCD PLUS
✓. At least 1 diagnostic test consistent with PCD:

What they're measuring

Mean FEV1 Percent Predicted Values in Well State and Sick State

Timeframe: 12 months

Mean Primary Ciliary Dyskinesia-Quality of Life Score in Well State and Sick State

Timeframe: 12 months

Mean PCD-Respiratory Symptom Diary Score Well State and Sick State

Timeframe: 12 months

Trial details

NCT IDNCT05161858

SponsorUniversity of North Carolina, Chapel Hill

Sponsor typeOTHER

Study typeOBSERVATIONAL

Primary completion2025-09-30

View on ClinicalTrials.gov More Primary Ciliary Dyskinesia trials