This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with DMD. The maximum participant duration for this study is 156 weeks.
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Part 1 (Cohorts 1 to 5): Change from Baseline in Quantity of Delandistrogene Moxeparvovec Dystrophin Expression at Week 12, as Measured by Western Blot
Timeframe: Baseline, Week 12
Part 1 (Cohorts 6 to 8): Quantity of Delandistrogene Moxeparvovec Dystrophin Expression at Week 12 as Measured by Western Blot
Timeframe: Week 12
Cohort 8: Number of Participants with Acute Liver Injury (ALI)
Timeframe: Baseline up to Week 72
Sarepta Therapeutics Inc., For Clinical Trial Information, Select Option 4