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Telomeric 22Q13 Monosomy Syndrome
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Telomeric 22Q13 Monosomy Syndrome trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Telomeric 22Q13 Monosomy Syndrome trials may be worth asking aboutNorth America
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This Phase 3, randomized, double-blind, parallel-group (2-arm), placebo-controlled, multicenter study will evaluate the efficacy and safety of NNZ-2591 compared…
This Phase 3, open-label extension, multicenter study will evaluate long-term safety, tolerability and efficacy of NNZ-2591 in pediatric participants with Phela…
This is a Phase 1/2, first in human, open-label, dose-escalation study to evaluate the safety, tolerability, and clinical activity of a single dose of JAG201 ad…
The purpose of this study is to comprehensively characterize PMS using standardized medical, cognitive, and behavioral measures and to track the natural history…
This is an open-label, dose-escalation study to evaluate the safety, tolerability, and clinical activity of a single dose of RB001 administered via intracerebro…