Adult Polyglucosan Body Disease

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Adult Polyglucosan Body Disease trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingNot Applicable

NCT02683512

GBE Deficiency (GSD IV and APBD) Natural History Study

Collection and review of clinical information related to glycogen branching enzyme (GBE) deficiency, diagnosed as Glycogen Storage Disease Type IV (GSD IV) or A…

United States200 participantsStarted 2015-12

Treatment: No intervention

All recent trials (2 shown)

CompletedPhase 2

NCT00947960

Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease

The purpose of the study is to determine if triheptanoin is an effective treatment for the symptoms of Adult Polyglucosan Body Disease.

France23 participantsStarted 2009-06

Treatment: Triheptanoin, Vegetable Oil